Landmark gene editing creates a medicine made for just one patient

It is the first time the treatment has been personalised for one human's DNA.
Dr Martin Pal (PhD).
Dr Martin Pal (PhD).

CRISPR technology has shown strong results treating a baby with a life-threatening liver cell mutation, with scientists saying it is the first documented use of personalised gene-editing treatment.

US scientists say they have treated a boy named KJ Muldoon who had severe carbamoyl-phosphate synthetase 1 (CPS1) deficiency, diagnosed 48 hours after birth.